Exploring non-coding variants and evaluation of antisense oligonucleotides for splicing redirection in Usher syndrome

Autor: García-Bohórquez, Belén, Barberán-Martínez, Pilar, Aller, Elena, Jaijo, Teresa, Mínguez, Pablo, Rodilla, Cristina, Fernández-Caballero, Lidia, Blanco-Kelly, Fiona, Ayuso, Carmen, Sanchis-Juan, Alba, Broekman, Sanne, de Vrieze, Erik, van Wijk, Erwin, García-García, Gema, Millán, José M.
Zdroj: In Molecular Therapy - Nucleic Acids 10 December 2024 35(4)
Databáze: ScienceDirect