Cas9 editing of ATXN1 in a spinocerebellar ataxia type 1 mice and human iPSC-derived neurons

Autor: Fagan, Kelly J., Chillon, Guillem, Carrell, Ellie M., Waxman, Elisa A., Davidson, Beverly L.
Zdroj: In Molecular Therapy - Nucleic Acids 10 December 2024 35(4)
Databáze: ScienceDirect