Functional benefit of CRISPR-Cas9-induced allele deletion for RYR1 dominant mutation

Autor: Beaufils, Mathilde, Melka, Margaux, Brocard, Julie, Benoit, Clement, Debbah, Nagi, Mamchaoui, Kamel, Romero, Norma B., Dalmas-Laurent, Anne Frédérique, Quijano-Roy, Susana, Fauré, Julien, Rendu, John, Marty, Isabelle
Zdroj: In Molecular Therapy - Nucleic Acids 10 September 2024 35(3)
Databáze: ScienceDirect