Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47phox-deficient chronic granulomatous disease

Autor: Siow, Kah Mun, Güngör, Merve, Wrona, Dominik, Raimondi, Federica, Pastukhov, Oleksandr, Tsapogas, Panagiotis, Menzi, Timon, Schmitz, Michael, Kulcsár, Péter István, Schwank, Gerald, Schulz, Ansgar, Jinek, Martin, Modlich, Ute, Siler, Ulrich, Reichenbach, Janine
Zdroj: In Molecular Therapy - Nucleic Acids 10 September 2024 35(3)
Databáze: ScienceDirect