Effective AAV-mediated gene replacement therapy in retinal organoids modeling AIPL1-associated LCA4

Autor: Sai, Hali, Ollington, Bethany, Rezek, Farah O., Chai, Niuzheng, Lane, Amelia, Georgiadis, Anastasios, Bainbridge, James, Michaelides, Michel, Sacristan-Reviriego, Almudena, Perdigão, Pedro R.L., Leung, Amy, van der Spuy, Jacqueline
Zdroj: In Molecular Therapy - Nucleic Acids 12 March 2024 35(1)
Databáze: ScienceDirect