Preclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic LZTR1 variants
| Autor: | Knauer, Carolin, Haltern, Henrike, Schoger, Eric, Kügler, Sebastian, Roos, Lennart, Zelarayán, Laura C., Hasenfuss, Gerd, Zimmermann, Wolfram-Hubertus, Wollnik, Bernd, Cyganek, Lukas |
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| Zdroj: | In Molecular Therapy - Nucleic Acids 12 March 2024 35(1) |
| Databáze: | ScienceDirect |
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