Single intravitreal administration of a tetravalent siRNA exhibits robust and efficient gene silencing in mouse and pig photoreceptors

Autor: Cheng, Shun-Yun, Caiazzi, Jillian, Biscans, Annabelle, Alterman, Julia F., Echeverria, Dimas, McHugh, Nicholas, Hassler, Matthew, Jolly, Samson, Giguere, Delaney, Cipi, Joris, Khvorova, Anastasia, Punzo, Claudio
Zdroj: In Molecular Therapy - Nucleic Acids 12 March 2024 35(1)
Databáze: ScienceDirect