In vivo genome editing using 244-cis LNPs and low-dose AAV achieves therapeutic threshold in hemophilia A mice
| Autor: | Han, Jeong Pil, Lee, Yeji, Lee, Jeong Hyeon, Chung, Hye Yoon, Lee, Geon Seong, Nam, Yu Ri, Choi, Myeongjin, Moon, Kyoung-Sik, Lee, Haeshin, Lee, Hyukjin, Yeom, Su Cheong |
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| Zdroj: | In Molecular Therapy - Nucleic Acids 12 December 2023 34 |
| Databáze: | ScienceDirect |
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