The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of neuromuscular disorders

Autor: Li, Xiang, Kheirabadi, Mahboubeh, Dougherty, Patrick G., Kamer, Kimberli J., Shen, Xiulong, Estrella, Nelsa L., Peddigari, Suresh, Pathak, Anushree, Blake, Sara L., Sizensky, Emmanuelle, Genio, Carmen del, Gaur, Arti B., Dhanabal, Mohanraj, Girgenrath, Mahasweta, Sethuraman, Natarajan, Qian, Ziqing
Zdroj: In Molecular Therapy - Nucleic Acids 12 September 2023 33:273-285
Databáze: ScienceDirect