Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C

Autor: Martinez-Navajas, Gonzalo, Ceron-Hernandez, Jorge, Simon, Iris, Lupiañez, Pablo, Diaz-McLynn, Sofia, Perales, Sonia, Modlich, Ute, Guerrero, Jose A., Martin, Francisco, Sevivas, Teresa, Lozano, Maria L., Rivera, Jose, Ramos-Mejia, Veronica, Tersteeg, Claudia, Real, Pedro J.
Zdroj: In Molecular Therapy - Nucleic Acids June 2023
Databáze: ScienceDirect