Protracted CLN3 Batten disease in mice that genetically model an exon-skipping therapeutic approach
| Autor: | Centa, Jessica L., Stratton, Matthew P., Pratt, Melissa A., Osterlund Oltmanns, Jenna R., Wallace, Douglas G., Miller, Steven A., Weimer, Jill M., Hastings, Michelle L. |
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| Zdroj: | In Molecular Therapy - Nucleic Acids 12 September 2023 33:15-27 |
| Databáze: | ScienceDirect |
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