Systemic delivery of a DUX4 targeting antisense oligonucleotide to treat Facioscapulohumeral Muscular Dystrophy
| Autor: | Bouwman, Linde F., den Hamer, Bianca, van den Heuvel, Anita, Franken, Marnix, Jackson, Michaela, Dwyer, Chrissa A., Tapscott, Stephen J., Rigo, Frank, van der Maarel, Silvère M., de Greef, Jessica C. |
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| Zdroj: | In Molecular Therapy - Nucleic Acids September 2021 |
| Databáze: | ScienceDirect |
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