BB-301: a silence and replace AAV-based vector for the treatment of oculopharyngeal muscular dystrophy
| Autor: | Strings-Ufombah, Vanessa, Malerba, Alberto, Kao, Shih-Chu, Harbaran, Sonal, Roth, Fanny, Cappellari, Ornella, Lu-Nguyen, Ngoc, Takahashi, Keiko, Mukadam, Sophie, Kilfoil, Georgina, Kloth, Claudia, Roelvink, Petrus, Dickson, George, Trollet, Capucine, Suhy, David |
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| Zdroj: | In Molecular Therapy - Nucleic Acids 4 June 2021 24:67-78 |
| Databáze: | ScienceDirect |
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