Allele-Specific CRISPR/Cas9 Correction of a Heterozygous DNM2 Mutation Rescues Centronuclear Myopathy Cell Phenotypes
| Autor: | Rabai, Aymen, Reisser, Léa, Reina-San-Martin, Bernardo, Mamchaoui, Kamel, Cowling, Belinda S., Nicot, Anne-Sophie, Laporte, Jocelyn |
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| Zdroj: | In Molecular Therapy - Nucleic Acids 7 June 2019 16:246-256 |
| Databáze: | ScienceDirect |
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