Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD
| Autor: | Akpulat, Ugur, Wang, Haicui, Becker, Kerstin, Contreras, Adriana, Partridge, Terence A., Novak, James S., Cirak, Sebahattin |
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| Zdroj: | In Molecular Therapy - Nucleic Acids 7 December 2018 13:534-542 |
| Databáze: | ScienceDirect |
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