Lentiviral gene therapy with IGF2-tagged GAA normalizes the skeletal muscle proteome in murine Pompe disease
| Autor: | Liang, Qiushi, Vlaar, Eva C., Pijnenburg, Joon M., Rijkers, Erikjan, Demmers, Jeroen A.A., Vulto, Arnold G., van der Ploeg, Ans T., van Til, Niek P., Pijnappel, W.W.M. Pim |
|---|---|
| Zdroj: | In Journal of Proteomics 16 January 2024 291 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect