Safety and efficacy of ivacaftor in infants aged 1 to less than 4 months with cystic fibrosis

Autor: McNally, Paul, Singh, Alvin, McColley, Susanna A., Davies, Jane C., Higgins, Mark, Liu, Meng, Lu, Jennifer, Rodriguez-Romero, Violeta, Shih, Judy L., Rosenfeld, Margaret
Zdroj: In Journal of Cystic Fibrosis May 2024 23(3):429-435
Databáze: ScienceDirect