116 First-in-human clinical trial with SPL84, an antisense oligonucleotide for treatment of people with cystic fibrosis with the 3849 +10 Kb C - > T mutation

Autor: Caraco, Y., Wanounou, M., Friedman, L., Cohen, A., Hart, G., Kerem, E.
Zdroj: In Journal of Cystic Fibrosis October 2023 22 Supplement 3:S61-S61
Databáze: ScienceDirect