Antisense oligonucleotide splicing modulation as a novel Cystic Fibrosis therapeutic approach for the W1282X nonsense mutation
| Autor: | Oren, Yifat S., Avizur-Barchad, Ofra, Ozeri-Galai, Efrat, Elgrabli, Renana, Schirelman, Meital R., Blinder, Tehilla, Stampfer, Chava D., Ordan, Merav, Laselva, Onofrio, Cohen-Cymberknoh, Malena, Kerem, Eitan, Bear, Christine E, Kerem, Batsheva |
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| Zdroj: | In Journal of Cystic Fibrosis July 2022 21(4):630-636 |
| Databáze: | ScienceDirect |
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