592: Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR/Cas9 gene editing

Autor: Hart, S., Walker, A., Woodall, M., Maeshima, R., Pearce, D., O’Hara-Wright, M., Sanz, D., Guerrini, I., Aldossary, A., O’Callaghan, C., Baines, D., McAnulty, R., Harrison, P.
Zdroj: In Journal of Cystic Fibrosis November 2021 20 Supplement 2:S281-S282
Databáze: ScienceDirect