Three-year outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A

Autor: Madan, Bella 1, ∗, Ozelo, Margareth C. 2, Raheja, Priyanka 3, Symington, Emily 4, Quon, Doris V. 5, Leavitt, Andrew D. 6, Pipe, Steven W. 7, Lowe, Gillian 8, Kenet, Gili 9, Reding, Mark T. 10, Mason, Jane 11, 12, Wang, Michael 13, von Drygalski, Annette 14, Klamroth, Robert 15, 16, Shapiro, Susan 17, 18, 19, Chambost, Hervé 20, Dunn, Amy L. 21, Oldenburg, Johannes 22, Chou, Sheng-Chieh 23, Peyvandi, Flora 24, 25, Millar, Carolyn M. 26, 27, Osmond, Dane 28, Yu, Hua 28, Dashiell-Aje, Ebony 28, Robinson, Tara M. 28, Mahlangu, Johnny 29
Zdroj: In Journal of Thrombosis and Haemostasis July 2024 22(7):1880-1893
Databáze: ScienceDirect