Hemophilia gene therapy: first, do no harm

Autor: Valentino, Leonard A., Kaczmarek, Radoslaw, Pierce, Glenn F., Noone, Declan, O’Mahony, Brian, Page, David, Rotellini, Dawn, Skinner, Mark W.
Zdroj: In Journal of Thrombosis and Haemostasis September 2023 21(9):2354-2361
Databáze: ScienceDirect