A review of the rationale for gene therapy for hemophilia A with inhibitors: one-shot tolerance and treatment?

Autor: Valentino, Leonard A., Ozelo, Margareth C., Herzog, Roland W., Key, Nigel S., Pishko, Allyson M., Ragni, Margaret V., Samelson-Jones, Benjamin J., Lillicrap, David
Zdroj: In Journal of Thrombosis and Haemostasis November 2023 21(11):3033-3044
Databáze: ScienceDirect