Promoting translational readthrough of nonsense mutations in cystic fibrosis mouse model: Assessing the biodistribution and efficacy of the NV848 1,2,4-oxadiazole compound for the rescue of CFTR protein expression
| Autor: | Fiduccia, Ignazio, Corrao, Federica, Zizzo, Maria Grazia, Perriera, Riccardo, Genovese, Francesco, Vitale, Emanuele, Ricci, Davide, Melfi, Raffaella, Tutone, Marco, Pace, Andrea, Lentini, Laura, Pibiri, Ivana |
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| Zdroj: | In Molecular Therapy October 2024 |
| Databáze: | ScienceDirect |
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