Engineering memory T cells as a platform for long-term enzyme replacement therapy in lysosomal storage disorders

Autor: Kleinboehl, Evan W., Laoharawee, Kanut, Jensen, Jacob D., Peterson, Joseph J., Slipek, Nicholas J., Wick, Bryce J., Johnson, Matthew J., Webber, Beau R., Moriarity, Branden S.
Zdroj: In Molecular Therapy September 2024
Databáze: ScienceDirect