Safety and efficacy studies of CRISPR-Cas9 treatment of sickle cell disease highlights disease-specific responses
| Autor: | Frati, Giacomo, Brusson, Megane, Sartre, Gilles, Mlayah, Bochra, Felix, Tristan, Chalumeau, Anne, Antoniou, Panagiotis, Hardouin, Giulia, Concordet, Jean-Paul, Romano, Oriana, Turchiano, Giandomenico, Miccio, Annarita |
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| Zdroj: | In Molecular Therapy 4 December 2024 32(12):4337-4352 |
| Databáze: | ScienceDirect |
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