Safety and efficacy studies of CRISPR-Cas9 treatment of sickle cell disease highlights disease-specific responses

Autor: Frati, Giacomo, Brusson, Megane, Sartre, Gilles, Mlayah, Bochra, Felix, Tristan, Chalumeau, Anne, Antoniou, Panagiotis, Hardouin, Giulia, Concordet, Jean-Paul, Romano, Oriana, Turchiano, Giandomenico, Miccio, Annarita
Zdroj: In Molecular Therapy July 2024
Databáze: ScienceDirect