AAV-mediated gene therapy for sialidosis

Autor: van de Vlekkert, Diantha, Hu, Huimin, Weesner, Jason A., Fremuth, Leigh E., Brown, Scott A., Lu, Meifen, Gomero, Elida, Campos, Yvan, Sheppard, Heather, d’Azzo, Alessandra
Zdroj: In Molecular Therapy 3 July 2024 32(7):2094-2112
Databáze: ScienceDirect