In vivo adenine base editing rescues adrenoleukodystrophy in a humanized mouse model

Autor: Gopalappa, Ramu, Lee, MinYoung, Kim, Globinna, Jung, Eul Sik, Lee, Hanahrae, Hwang, Hye-Yeon, Lee, Jong Geol, Kim, Su Jung, Yoo, Hyun Ju, Sung, Young Hoon, Kim, Daesik, Baek, In-Jeoung, Kim, Hyongbum Henry
Zdroj: In Molecular Therapy 3 July 2024 32(7):2190-2206
Databáze: ScienceDirect