In vivo base editing of a pathogenic Eif2b5 variant improves vanishing white matter phenotypes in mice
| Autor: | Böck, Desirée, Revers, Ilma M., Bomhof, Anastasia S.J., Hillen, Anne E.J., Boeijink, Claire, Kissling, Lucas, Egli, Sabina, Moreno-Mateos, Miguel A., van der Knaap, Marjo S., van Til, Niek P., Schwank, Gerald |
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| Zdroj: | In Molecular Therapy 1 May 2024 32(5):1328-1343 |
| Databáze: | ScienceDirect |
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