Improved efficacy of FKRP AAV gene therapy by combination with ribitol treatment for LGMD2I
| Autor: | Cataldi, Marcela P., Vannoy, Charles H., Blaeser, Anthony, Tucker, Jason D., Leroy, Victoria, Rawls, Raegan, Killilee, Jessalyn, Holbrook, Molly C., Lu, Qi Long |
|---|---|
| Zdroj: | In Molecular Therapy 6 December 2023 31(12):3478-3489 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|