RNA base editing therapy cures hearing loss induced by OTOF gene mutation
Autor: | Xue, Yuanyuan, Tao, Yong, Wang, Xing, Wang, Xueling, Shu, Yilai, Liu, Yuanhua, Kang, Wen, Chen, Sifan, Cheng, Zhenzhe, Yan, Boou, Xie, Yanwei, Bi, Lanting, Jia, Haitao, Li, Jinhui, Xiao, Qingquan, Chen, Liying, Yao, Xuan, Shi, Linyu, Yang, Hui, Wu, Hao |
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Zdroj: | In Molecular Therapy 6 December 2023 31(12):3520-3530 |
Databáze: | ScienceDirect |
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