RNA base editing therapy cures hearing loss induced by OTOF gene mutation

Autor: Xue, Yuanyuan, Tao, Yong, Wang, Xing, Wang, Xueling, Shu, Yilai, Liu, Yuanhua, Kang, Wen, Chen, Sifan, Cheng, Zhenzhe, Yan, Boou, Xie, Yanwei, Bi, Lanting, Jia, Haitao, Li, Jinhui, Xiao, Qingquan, Chen, Liying, Yao, Xuan, Shi, Linyu, Yang, Hui, Wu, Hao
Zdroj: In Molecular Therapy 6 December 2023 31(12):3520-3530
Databáze: ScienceDirect