Intravitreal injection of a rationally designed AAV capsid library in non-human primate identifies variants with enhanced retinal transduction and neutralizing antibody evasion
Autor: | Kellish, Patrick C., Marsic, Damien, Crosson, Sean M., Choudhury, Shreyasi, Scalabrino, Miranda L., Strang, Christianne E., Hill, Julie, McCullough, K. Tyler, Peterson, James J., Fajardo, Diego, Gupte, Siddhant, Makal, Victoria, Kondratov, Oleksandr, Kondratova, Liudmyla, Iyer, Siva, Witherspoon, C. Douglas, Gamlin, Paul D., Zolotukhin, Sergei, Boye, Sanford L., Boye, Shannon E. |
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Zdroj: | In Molecular Therapy 6 December 2023 31(12):3441-3456 |
Databáze: | ScienceDirect |
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