A promoterless AAV6.2FF-based lung gene editing platform for the correction of surfactant protein B deficiency
| Autor: | Thomas, Sylvia P., Domm, Jakob M., van Vloten, Jacob P., Xu, Liqun, Vadivel, Arul, Yates, Jacob G.E., Pei, Yanlong, Ingrao, Joelle, van Lieshout, Laura P., Jackson, Sergio R., Minott, Jessica A., Achuthan, Adithya, Mehrani, Yeganeh, McAusland, Thomas M., Zhang, Wei, Karimi, Khalil, Vaughan, Andrew E., de Jong, Jondavid, Kang, Martin H., Thebaud, Bernard, Wootton, Sarah K. |
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| Zdroj: | In Molecular Therapy 6 December 2023 31(12):3457-3477 |
| Databáze: | ScienceDirect |
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