Engineered arylsulfatase A with increased activity, stability and brain delivery for therapy of metachromatic leukodystrophy

Autor: Yaghootfam, Claudia, Sylvester, Marc, Turk, Boris, Gieselmann, Volkmar, Matzner, Ulrich
Zdroj: In Molecular Therapy 4 October 2023 31(10):2962-2974
Databáze: ScienceDirect