Preclinical evaluation of ADVM-062, a novel intravitreal gene therapy vector for the treatment of blue cone monochromacy

Autor: Hanna, Kelly, Nieves, Julio, Dowd, Christine, Bender, Kristina Oresic, Sharma, Pallavi, Singh, Baljit, Renz, Mark, Ver Hoeve, James N., Cepeda, Diana, Gelfman, Claire M., Riley, Brigit E., Grishanin, Ruslan N.
Zdroj: In Molecular Therapy 5 July 2023 31(7):2014-2027
Databáze: ScienceDirect