Phase I study of liver depot gene therapy in late-onset Pompe disease
| Autor: | Smith, Edward C., Hopkins, Sam, Case, Laura E., Xu, Ming, Walters, Crista, Dearmey, Stephanie, Han, Sang-oh, Spears, Tracy G., Chichester, Jessica A., Bossen, Edward H., Hornik, Christoph P., Cohen, Jennifer L., Bali, Deeksha, Kishnani, Priya S., Koeberl, Dwight D. |
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| Zdroj: | In Molecular Therapy 5 July 2023 31(7):1994-2004 |
| Databáze: | ScienceDirect |
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