Development of a double shmiR lentivirus effectively targeting both BCL11A and ZNF410 for enhanced induction of fetal hemoglobin to treat β-hemoglobinopathies

Autor: Liu, Boya, Brendel, Christian, Vinjamur, Divya S., Zhou, Yu, Harris, Chad, McGuinness, Meaghan, Manis, John P., Bauer, Daniel E., Xu, Haiming, Williams, David A.
Zdroj: In Molecular Therapy 3 August 2022 30(8):2693-2708
Databáze: ScienceDirect