Development of a double shmiR lentivirus effectively targeting both BCL11A and ZNF410 for enhanced induction of fetal hemoglobin to treat β-hemoglobinopathies
Autor: | Liu, Boya, Brendel, Christian, Vinjamur, Divya S., Zhou, Yu, Harris, Chad, McGuinness, Meaghan, Manis, John P., Bauer, Daniel E., Xu, Haiming, Williams, David A. |
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Zdroj: | In Molecular Therapy 3 August 2022 30(8):2693-2708 |
Databáze: | ScienceDirect |
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