Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
Autor: | Bersani, Margherita, Rizzuti, Mafalda, Pagliari, Elisa, Garbellini, Manuela, Saccomanno, Domenica, Moulton, Hong M., Bresolin, Nereo, Comi, Giacomo P., Corti, Stefania, Nizzardo, Monica |
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Zdroj: | In Molecular Therapy 2 March 2022 30(3):1288-1299 |
Databáze: | ScienceDirect |
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