Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease
| Autor: | Li, Yedda, Miller, Christopher A., Shea, Lauren K., Jiang, Xuntian, Guzman, Miguel A., Chandler, Randy J., Ramakrishnan, Sai M., Smith, Stephanie N., Venditti, Charles P., Vogler, Carole A., Ory, Daniel S., Ley, Timothy J., Sands, Mark S. |
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| Zdroj: | In Molecular Therapy 3 February 2021 29(2):691-701 |
| Databáze: | ScienceDirect |
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