RNAi-Based Gene Therapy Rescues Developmental and Epileptic Encephalopathy in a Genetic Mouse Model

Autor: Aimiuwu, Osasumwen V., Fowler, Allison M., Sah, Megha, Teoh, Jia Jie, Kanber, Ayla, Pyne, Nettie K., Petri, Sabrina, Rosenthal-Weiss, Chana, Yang, Mu, Harper, Scott Q., Frankel, Wayne N.
Zdroj: In Molecular Therapy 8 July 2020 28(7):1706-1716
Databáze: ScienceDirect