CRISPR-Induced Deletion with SaCas9 Restores Dystrophin Expression in Dystrophic Models In Vitro and In Vivo

Autor: Duchêne, Benjamin L., Cherif, Khadija, Iyombe-Engembe, Jean-Paul, Guyon, Antoine, Rousseau, Joel, Ouellet, Dominique L., Barbeau, Xavier, Lague, Patrick, Tremblay, Jacques P.
Zdroj: In Molecular Therapy 7 November 2018 26(11):2604-2616
Databáze: ScienceDirect