In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model

Autor: Mattar, Citra N.Z., Gil-Farina, Irene, Rosales, Cecilia, Johana, Nuryanti, Tan, Yvonne Yi Wan, McIntosh, Jenny, Kaeppel, Christine, Waddington, Simon N., Biswas, Arijit, Choolani, Mahesh, Schmidt, Manfred, Nathwani, Amit C., Chan, Jerry K.Y.
Zdroj: In Molecular Therapy 2 August 2017 25(8):1843-1853
Databáze: ScienceDirect