Gender-Specific Amelioration of SMA Phenotype upon Disruption of a Deep Intronic Structure by an Oligonucleotide
Autor: | Howell, Matthew D., Ottesen, Eric W., Singh, Natalia N., Anderson, Rachel L., Singh, Ravindra N. |
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Zdroj: | In Molecular Therapy 7 June 2017 25(6):1328-1341 |
Databáze: | ScienceDirect |
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