125. Engineered Nucleases-Mediated In Situ Correction of a Genetic Defect By Homologous Recombination Into the Native Locus

Autor: Carmela Latella, Maria, Miselli, Francesca, Turchiano, Giandomenico, Mussolino, Claudio, Cudeiro, Javier, Larcher, Fernando, Recchia, Alessandra
Zdroj: In Molecular Therapy May 2015 23 Supplement 1:S51-S52
Databáze: ScienceDirect