439. Prolonged Expression of Secreted Enzymes in Dogs After Liver Delivery of Sleeping Beauty Transposons: Implications for Non-Viral Gene Therapy of Mucopolysaccharidoses Types I and VII

Autor: Aronovich, Elena L., Hyland, Kendra A., Hall, Bryan C., Bell, Jason B., Olson, Erik R., Rusten, Myra, Hunter, David W., Whitley, Chester B., Ellinwood, N. Matthew, McIvor, R. Scott, Hackett, Perry B.
Zdroj: In Molecular Therapy May 2016 24 Supplement 1:S174-S174
Databáze: ScienceDirect