328. Proof-of-Principle Study Shows Efficient Skipping of Exon 2 Using Antisense Morpholino Oligomers

Autor: Simmons, Tabatha R., Wein, Nicolas, Gumienny, Felecia, Huang, Hannah, Flanigan, Kevin M.
Zdroj: In Molecular Therapy May 2016 24 Supplement 1:S131-S131
Databáze: ScienceDirect