162. Functional Correction of Mucopolysaccharidosis I in Adult Mice by a Systemic rAAV9-IDUA Gene Delivery
| Autor: | Meadows, Aaron, Pineda, Ricardo, Camboni, Marybeth, Waligura, Kathryn, Murrey, Darren, McCarty, Douglas M., Fu, Haiyan |
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| Zdroj: | In Molecular Therapy May 2016 24 Supplement 1:S64-S64 |
| Databáze: | ScienceDirect |
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