Sustained Enzymatic Correction by rAAV-Mediated Liver Gene Therapy Protects Against Induced Motor Neuropathy in Acute Porphyria Mice
| Autor: | Unzu, Carmen, Sampedro, Ana, Mauleón, Itsaso, Alegre, Manuel, Beattie, Stuart G, de Salamanca, Rafael Enríquez, Snapper, Jolanda, Twisk, Jaap, Petry, Harald, González-Aseguinolaza, Gloria, Artieda, Julio, Rodríguez-Pena, María Sol, Prieto, Jesús, Fontanellas, Antonio |
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| Zdroj: | In Molecular Therapy February 2011 19(2):243-250 |
| Databáze: | ScienceDirect |
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