Adeno-associated Virus 9 Mediated FKRP Gene Therapy Restores Functional Glycosylation of α-dystroglycan and Improves Muscle Functions

Autor: Xu, Lei, Lu, Pei Juan, Wang, Chi-Hsien, Keramaris, Elizabeth, Qiao, Chunping, Xiao, Bin, Blake, Derek J, Xiao, Xiao, Lu, Qi Long
Zdroj: In Molecular Therapy October 2013 21(10):1832-1840
Databáze: ScienceDirect