Infectious Delivery and Expression of a 135 kb Human FRDA Genomic DNA Locus Complements Friedreich's Ataxia Deficiency in Human Cells

Autor: Gomez-Sebastian, Silvia, Gimenez-Cassina, Alfredo, Diaz-Nido, Javier, Lim, Filip, Wade-Martins, Richard
Zdroj: In Molecular Therapy February 2007 15(2):248-254
Databáze: ScienceDirect